Novartis' Zolgensma gene therapy study halted on animal safety concerns

Novartis' Zolgensma gene therapy study halted on animal safety concerns

Novartis’ Zolgensma gene therapy study halted by FDA on animal safety concerns

By ADAM FEUERSTEIN

DOMINICK REUTER/AFP/GETTY IMAGES

The hold affects the clinical trial that was testing a higher dose administered by spinal injection to older children with spinal muscular atrophy.

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