domingo, 10 de diciembre de 2023

In historic decision, FDA approves a CRISPR-based medicine for treatment of sickle cell disease A Feurstein, StatNews, December 8, 2023 (Posted Dec 08, 2023 2PM)

https://phgkb.cdc.gov/PHGKB/phgHome.action?action=home From the article: "The Food and Drug Administration on Friday approved the world’s first medicine based on CRISPR gene-editing technology, a groundbreaking treatment for sickle cell disease that delivers a potential cure for people born with the chronic and life-shortening blood disorder. The new medicine, called Casgevy,'s authorization is a scientific triumph for the technology that can efficiently and precisely repair DNA mutations — ushering in a new era of genetic medicines for inherited diseases. "

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