Wary hemophilia patients are willing to wait longer for a safe gene therapy

Wary hemophilia patients are willing to wait longer for a safe gene therapy

Wary hemophilia patients say they’re willing to wait longer for a safe gene therapy

By ELIZABETH COONEY

ADOBE

For one family active in the hemophilia patient community, the FDA rejection of BioMarin's gene therapy was disappointing, but also appreciated. 

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