Pfizer, with hopeful results, leaps into race for a Duchenne gene therapy

Pfizer, with hopeful results, leaps into race for a Duchenne gene therapy

STAT Plus: Pfizer, with early but hopeful results, leaps into the race for a Duchenne gene therapy

By MATTHEW HERPER

RUBY WALLAU FOR STAT

The company’s gene therapy appeared to help children with the condition, but its side effects were severe in some clinical trial participants.

READ MORE