martes, 26 de noviembre de 2019

Global Blood's novel sickle cell drug approved

The Readout
Damian Garde

Global Blood's novel sickle cell drug approved

The FDA yesterday approved a new, once-daily drug to treat sickle cell disease that has a unique mechanism: It boosts hemoglobin, and by extension oxygen transport, in the bloodstream. The drug, called Oxbryta, was developed by Global Blood Therapeutics — and achieved approval three months earlier than projected. 

It will cost $125,000 per year before discounts.

For a long time, there were few options for patients with sickle cell disease. That’s changing: Several gene therapies are in the works, and the FDA approved a monoclonal antibody drug from Novartis called crizanlizumab, or Adakveo, just a couple days ago.

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