Sarepta gene therapy improves muscle function in rare limb-girdle disease

Sarepta gene therapy improves muscle function in rare limb-girdle disease

STAT Plus: Sarepta gene therapy improves muscle function for patients with rare limb-girdle disease

By ADAM FEUERSTEIN

KRISTOFFER TRIPPLAAR/SIPA VIA AP

Sarepta Therapeutics said three patients with limb-girdle muscular dystrophy showed improvements after a one-time infusion of an experimental gene therapy.

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